Project Title: A Disruptive Gene Therapy Platform, Replacing viruses in the Treatment of Genetic Conditions (DTIF)
Thematic Area: Rare Skin Diseases Focus of Research: Gene Therapy
Group Team members: Dr Ruth Foley, Dr Qian Xu, Dr Dario Sandoval Manzanares, Dr Mihai Negru, Bei Qiu
Overview: This project aims to use novel non-viral, polymer-based gene therapy, with the potential to treat a broad range of severe genetic conditions. The first proof of concept therapy has been designed for the devastating genetic skin disease Epidermolysis Bullosa (EB), with the next target being Cystic Fibrosis
Funded by: EB Research Partnership Inc.
PI: Prof. Wenxin Wang
Project Duration: December 2019-December 2022